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Clinical trials in pediatric ALS: a TRICALS feasibility study

dc.date.accessioned2023-02-09T18:18:57Z
dc.date.available2023-02-09T18:18:57Z
dc.date.created2022-03-08T12:12:46Z
dc.date.issued2022
dc.identifier.citationKliest, Tessa van Eijk, Ruben P. A. Al-Chalabi, Ammar Albanese, Alberto Andersen, Peter M. Amador, Maria Del Mar Bråthen, Geir Brunaud-Danel, Veronique Brylev, Lev Camu, William de Carvalho, Mamede Cereda, Cristina Cetin, Hakan Chaverri, Delia Chiò, Adriano Corcia, Philippe Couratier, Philippe De Marchi, Fabiola Desnuelle, Claude van Es, Michael A. Esteban, Jesús Filosto, Massimiliano Redondo, Alberto García Grosskreutz, Julian Hanemann, Clemens O. Holmøy, Trygve Høyer, Helle Ingre, Caroline Koritnik, Blaz Kuzma-Kozakiewicz, Magdalena Lambert, Thomas Leigh, Peter N. Lunetta, Christian Mandrioli, Jessica McDermott, Christopher J. Meyer, Thomas Mora, Jesus S. Petri, Susanne Povedano, Mónica Reviers, Evy Riva, Nilo Roes, Kit C. B. Rubio, Miguel Á. Salachas, François Sarafov, Stayko Sorarù, Gianni Stevic, Zorica Svenstrup, Kirsten Møller, Anette Torvin Turner, Martin R. Van Damme, Philip van Leeuwen, Lucie A. G. Varona, Luis Costa, Juan F. Vázquez Weber, Markus Hardiman, Orla Berg, Leonard H. van den . Clinical trials in pediatric ALS: a TRICALS feasibility study. Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration. 2022
dc.identifier.urihttp://hdl.handle.net/10852/99858
dc.description.abstractBackground: Pediatric investigation plans (PIPs) describe how adult drugs can be studied in children. In 2015, PIPs for Amyotrophic Lateral Sclerosis (ALS) became mandatory for European marketing-authorization of adult treatments, unless a waiver is granted by the European Medicines Agency (EMA).Objective: To assess the feasibility of clinical studies on the effect of therapy in children (
dc.description.abstractClinical trials in pediatric ALS: a TRICALS feasibility study
dc.languageEN
dc.publisherInforma healthcare
dc.rightsAttribution 4.0 International
dc.rights.urihttps://creativecommons.org/licenses/by/4.0/
dc.titleClinical trials in pediatric ALS: a TRICALS feasibility study
dc.title.alternativeENEngelskEnglishClinical trials in pediatric ALS: a TRICALS feasibility study
dc.typeJournal article
dc.creator.authorKliest, Tessa
dc.creator.authorvan Eijk, Ruben P. A.
dc.creator.authorAl-Chalabi, Ammar
dc.creator.authorAlbanese, Alberto
dc.creator.authorAndersen, Peter M.
dc.creator.authorAmador, Maria Del Mar
dc.creator.authorBråthen, Geir
dc.creator.authorBrunaud-Danel, Veronique
dc.creator.authorBrylev, Lev
dc.creator.authorCamu, William
dc.creator.authorde Carvalho, Mamede
dc.creator.authorCereda, Cristina
dc.creator.authorCetin, Hakan
dc.creator.authorChaverri, Delia
dc.creator.authorChiò, Adriano
dc.creator.authorCorcia, Philippe
dc.creator.authorCouratier, Philippe
dc.creator.authorDe Marchi, Fabiola
dc.creator.authorDesnuelle, Claude
dc.creator.authorvan Es, Michael A.
dc.creator.authorEsteban, Jesús
dc.creator.authorFilosto, Massimiliano
dc.creator.authorRedondo, Alberto García
dc.creator.authorGrosskreutz, Julian
dc.creator.authorHanemann, Clemens O.
dc.creator.authorHolmøy, Trygve
dc.creator.authorHøyer, Helle
dc.creator.authorIngre, Caroline
dc.creator.authorKoritnik, Blaz
dc.creator.authorKuzma-Kozakiewicz, Magdalena
dc.creator.authorLambert, Thomas
dc.creator.authorLeigh, Peter N.
dc.creator.authorLunetta, Christian
dc.creator.authorMandrioli, Jessica
dc.creator.authorMcDermott, Christopher J.
dc.creator.authorMeyer, Thomas
dc.creator.authorMora, Jesus S.
dc.creator.authorPetri, Susanne
dc.creator.authorPovedano, Mónica
dc.creator.authorReviers, Evy
dc.creator.authorRiva, Nilo
dc.creator.authorRoes, Kit C. B.
dc.creator.authorRubio, Miguel Á.
dc.creator.authorSalachas, François
dc.creator.authorSarafov, Stayko
dc.creator.authorSorarù, Gianni
dc.creator.authorStevic, Zorica
dc.creator.authorSvenstrup, Kirsten
dc.creator.authorMøller, Anette Torvin
dc.creator.authorTurner, Martin R.
dc.creator.authorVan Damme, Philip
dc.creator.authorvan Leeuwen, Lucie A. G.
dc.creator.authorVarona, Luis
dc.creator.authorCosta, Juan F. Vázquez
dc.creator.authorWeber, Markus
dc.creator.authorHardiman, Orla
dc.creator.authorBerg, Leonard H. van den
cristin.unitcode185,53,82,0
cristin.unitnameKlinikk for indremedisin og lab fag
cristin.ispublishedtrue
cristin.fulltextoriginal
cristin.qualitycode1
dc.identifier.cristin2008264
dc.identifier.bibliographiccitationinfo:ofi/fmt:kev:mtx:ctx&ctx_ver=Z39.88-2004&rft_val_fmt=info:ofi/fmt:kev:mtx:journal&rft.jtitle=Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration&rft.volume=&rft.spage=&rft.date=2022
dc.identifier.jtitleAmyotrophic Lateral Sclerosis and Frontotemporal Degeneration
dc.identifier.volume23
dc.identifier.issue7-8
dc.identifier.startpage481
dc.identifier.endpage488
dc.identifier.doihttps://doi.org/10.1080/21678421.2021.2024856
dc.type.documentTidsskriftartikkel
dc.type.peerreviewedPeer reviewed
dc.source.issn2167-8421
dc.type.versionPublishedVersion
dc.relation.projectHSØ/2021097
dc.relation.projectSTHF/8208.03 + 8208.04
dc.relation.projectALSNORGE/8208.05


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