Browsing Institutt for helse og samfunn by Author "Rasmussen, Magnhild"
Now showing items 1-2 of 2
-
Annexstad, Ellen Johanne; Fagerheim, Toril; Holm, Inger; Rasmussen, Magnhild (Journal article / Tidsskriftartikkel / PublishedVersion; Peer reviewed, 2019)Background: As new gene-related treatment options for Duchenne muscular dystrophy (DMD) are being developed, precise information about the patients’ genetic diagnosis and knowledge about the diversities of natural history ...
-
Magelssen, Morten; Rasmussen, Magnhild; Wallace, Sean; Førde, Reidun (Journal article / Tidsskriftartikkel / PublishedVersion; Peer reviewed, 2021)Background Nusinersen is one of an increasing number of new, expensive orphan drugs to receive authorization. These drugs strain public healthcare budgets and challenge principles for resource allocation. ...